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Brain Diseases, Metabolic, Inborn

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Brain Diseases, Metabolic, Inborn

Explore clinical trials studying Brain Diseases, Metabolic, Inborn. Study availability and eligibility vary by location and protocol.

948 public trials 197 recruiting studies

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Brain Diseases, Metabolic, Inborn trial results

Recruiting

A Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel

NCT06224413

Conditions: Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
Locations: Boston Children's Hospital Boston, Massachusetts, United States

Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States

UT Southwestern Medical Center Dallas, Texas, United States

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Recruiting

Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD

NCT07046338

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations: Shenzhen Geno-Immune Medical Institute Shenzhen, Guangdong, China

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Recruiting

The GBA Multimodal Study in Parkinson's Disease

NCT04101968

Conditions: Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +21 more
Locations: Oregon Health & Science University Portland, Oregon, United States

University of Washington Seattle, Washington, United States

Pacific Parkinson's Research Centre | University of British Columbia Vancouver, British Columbia, Canada

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Recruiting

Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford

NCT01793168

Conditions: 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
Locations: Sanford Health Sioux Falls, South Dakota, United States

Online Patient Enrollment System Sydney, Australia

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Recruiting

The Natural History of Sialidosis Type I

NCT06316752

Conditions: Bone Diseases, Bone Diseases, Metabolic, Brain Diseases, +15 more
Locations: National Taiwan University Hospital Taipei, Taiwan

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Recruiting

Drug Repurposing for Mitochondrial Disorders Using iPSCs Derived Neural Cells

NCT06967831

Conditions: Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +14 more
Locations: Universitätsklinikum Düsseldorf Düsseldorf, North Rhine-Westphalia, Germany

Charite - Universtaetsmedizin Berlin Berlin, State of Berlin, Germany

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Recruiting

Brain Aging in Phenylketonuria

NCT06969209

Conditions: Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +14 more
Locations: University Hospital Inselspital, Department of Diabetes, Endocrinology, Nutritional Medicine and Metabolism (UDEM) Bern, Switzerland

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Recruiting

Natural History of Sphingosine Phosphate Lyase Insufficiency Syndrome (SPLIS)

NCT06669949

Conditions: Addison Disease, Adrenal Gland Diseases, Adrenal Insufficiency, +47 more
Locations: University of California San Francisco San Francisco, California, United States

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Recruiting

Effect of the Mediterranean Diet in Patients Affected by CADASIL and Cerebral Amyloid Angiopathy.

NCT06933212

Conditions: Amyloidosis, Amyloidosis, Familial, Brain Diseases, +35 more
Locations: Fondazione IRCCS Istituto Neurologico Carlo Besta Milan, Italy

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Recruiting

Metabolic Control and Patient Well-being in Phenylketonuria: do Guidelines Make a Difference?

NCT05128149

Conditions: Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +9 more
Locations: University Childrens Hospital Zürich Zurich, Switzerland

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Brain Diseases, Metabolic, Inborn

Brain Diseases, Metabolic, Inborn trial results

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