Bone Marrow Failure Disorders

• Novartis Investigative Site — Toronto, Ontario, Canada
• Novartis Investigative Site — Nanning, Guangxi, China
• Novartis Investigative Site — Limassol, Cyprus
• Novartis Investigative Site — Al Mansurah, Egypt

• Duke University Medical Center Pediatric Blood and Marrow Transplant Program — Durham, North Carolina, United States

• Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo — Ribeirão Preto, São Paulo, Brazil

Not specified

• Joint Sino-US Clinical and Molecular Laboratory (JCML) — Shanghai, China

• Asan Medical Center - University of Ulsan College of Medicine — Seoul, South Korea

• UT MD Anderson Cancer Center — Houston, Texas, United States

• Asan Medical Center — Seoul, South Korea

• UCSF Comprehensive Cancer Center — San Francisco, California, United States

• University of California San Francisco — San Francisco, California, United States