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Clinical trial condition

Amino Acid Metabolism, Inborn Errors

Explore clinical trials studying Amino Acid Metabolism, Inborn Errors. Study availability and eligibility vary by location and protocol.

396 public trials 66 recruiting studies
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Amino Acid Metabolism, Inborn Errors trial results

Active, Not Recruiting

A Phase 1/Phase 2 Open-label Study to Evaluate the Safety, Tolerability, and Efficacy of a Single Intravenous Administration of SAR444836 in Adult Participants With Phenylketonuria

NCT05972629

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • University of California San Francisco- Site Number : 8400007 San Francisco, California, United States
  • Children's Hospital IMD Clinic- Site Number : 8400015 Aurora, Colorado, United States
  • University of Florida-Genetics- Site Number : 8400010 Gainesville, Florida, United States
  • UHCMC- Site Number : 8400014 Cleveland, Ohio, United States
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Active, Not Recruiting

AAV Gene Therapy Study for Subjects with PKU

NCT04480567

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
Locations
  • University of South Florida Tampa, Florida, United States
  • Morristown Medical Center Morristown, New Jersey, United States
  • University Hospital Birmingham NHS Foundation Trust Birmingham, United Kingdom
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Active, Not Recruiting

Pegtibatinase As an Enzyme Therapy for Patients with Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (COMPOSE)

NCT03406611

Conditions
Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
Locations
  • Travere Investigational Site - Virtual Site Culver City, California, United States
  • Travere Investigational Site Aurora, Colorado, United States
  • Travere Investigational Site Miami, Florida, United States
  • Travere Investigational Site Indianapolis, Indiana, United States
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