Completed
Long-term Efficacy and Safety of Lamazym for the Treatment of Patients With Alpha-Mannosidosis
NCT01681940
- Conditions
- Alpha-Mannosidosis, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +7 more
- Locations
-
- Kinderneurologie Metabole Ziekten, UZ Brussel, Laarbeeklaan 101 Brussels, Belgium
- Center for Metabolic Diseases, Department of Clinical Genetics, Juliane Marie Centre, Copenhagen University Hospital, Blegdamsvej 9 Copenhagen, Denmark
- Servicio de Pediatría, Hospital Materno Infantil, Reina Sofía, Avda Menéndez Pidal sn Córdoba, Spain
- Genetic Medicine, 6th floor, St Mary's Hospital, Oxford Road, Manchester, United Kingdom