Clinical trial discovery
Find Clinical Trials
Search studies by condition, treatment, location, eligibility, or trial identifier.
Showing 1–20 of 70 trials
Active filters
Clinical trials found
Published and searchable clinical trials
NCT07241234
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Indiana University Indianapolis, Indiana, United States
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
- University of Texas Southwestern Medical Center (UTSW) Dallas, Texas, United States
- Centrum Wsparcia Badań Klinicznych Pomorskiego Uniwersytetu Medycznego w Szczecinie Szczecin, West Pomeranian Voivodeship, Poland
NCT07728032
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Birmingham Children's Hospital Birmingham, United Kingdom
NCT06302348
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Indiana University School of Medicine Indianapolis, Indiana, United States
- Women and Children Hospital North Adelaide, Australia
- The Royal Children's Hospital Parkville, Australia
- Centre Hospitalier Universitaire (CHU) de Lille - Hôpital Jeanne de Flandre Lille, France
NCT07698743
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- CHRU de Nancy Nancy, France
NCT06971731
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- University of California Los Angeles (UCLA) School of Medicine Los Angeles, California, United States
- University of Florida (UF) Health Shands Hospital Gainesville, Florida, United States
- University of South Florida Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
GenSci144 Tablets Phase I Clinical Trial
NCT07685210
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- The First Affiliated Hospital of Shandong First Medical University (Shandong Qianfoshan Hospital). Jinan, Shandong, China
NCT06289348
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +18 more
- Locations
-
- Hôpital Necker Enfants Malades Paris, France
NCT07477691
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- UCLA Dept. of Human Genetics Los Angeles, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- University Of South Florida Medical Center Tampa, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
NCT01659749
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
-
- Emory University Department of Human Genetics Atlanta, Georgia, United States
NCT07526909
- Conditions
- Amino Acid Metabolism, Inborn Errors, Behavior, Brain Diseases, +12 more
- Locations
-
- Hacettepe University Ankara, Turkey (Türkiye)
GMP Powdered Substitutes in PKU and TYR
NCT06941532
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +12 more
- Locations
-
- Birmingham Women and Children's Hospital Birmingham, United Kingdom
Long-Term Follow Up Study of Subjects Previously Administered HMI 102
NCT04348708
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +11 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States
- Icahn School of Medicine at Mount Sinai New York, United States
A Trial to Examine if Repinatrabit is Processed Differently in Adults With Reduced Liver or Kidney Function Compared to Adults With Normal Liver and Kidney Function
NCT07713758
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
Not specified
NCT05781399
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- University of Florida College of Medicine Gainesville, Florida, United States
- University of South Florida Tampa, Florida, United States
- Rare Disease Research Atlanta, Georgia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
NCT05948020
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Children's Hospital of Fudan University Shanghai, China
NCT04879277
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Clinical investigation center, University Hospital, Tours Tours, France
- Internal Medicine Service, University Hospital, Tours Tours, France
NCT03939052
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- BC Children's Hospital Research Institute, University of British Columbia Vancouver, British Columbia, Canada
Evaluation of PKU Explore
NCT03168399
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +11 more
- Locations
-
- NHS Greater Glasgow and Clyde Glasgow, Lanarkshire, United Kingdom
- Birmingham Women's and Children's NHS Foundation Trust Burringham, West Midlands, United Kingdom
- Bradford Teaching Hospitals NHS Foundation Trust Bradford, West Yorkshire, United Kingdom
Evaluation of PKU Start
NCT03058848
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +11 more
- Locations
-
- NHS Greater Glasgow and Clyde Glasgow, Lanarkshire, United Kingdom
- Birmingham Children's Hospital NHS Foundation Trust Birmingham, West Midlands, United Kingdom
- Bradford Teaching Hospitals NHS Foundation Trust Bradford, West Yorkshire, United Kingdom
NCT05099640
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Stanford University Center for Academic Medicine Stanford, California, United States
- University of Colorado and the Children's Hospital CO Aurora, Colorado, United States
- UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism Gainesville, Florida, United States
- Indiana University School of Medicine Indianapolis, Indiana, United States