Recruiting
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
NCT07052929
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
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- Lurie Children's Hospital Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Oregon Health & Science University Portland, Oregon, United States
- The Hospital for Sick Children Toronto, Ontario, Canada