Active, Not Recruiting
An Open-label, Phase 1/2 Trial of Gene Therapy 4D-310 in Adults With Fabry Disease
NCT04519749
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- University of California at San Diego La Jolla, California, United States
- Emory University Atlanta, Georgia, United States
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
- Lysosomal & Rare Disorders Research & Treatment Center, Inc Fairfax, Virginia, United States