Not Yet Recruiting
Personalized Antisense Oligonucleotide for A Single Participant With PACS1 Gene Mutation Associated With Schuurs-Hoeijmakers Syndrome (SHMS)
NCT07474298
- Conditions
- Schuurs-Hoeijmakers Syndrome
- Locations
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- The Hospital for Sick Children (SickKids) Toronto, Ontario, Canada