Not yet recruiting
Single Injection of rAAV9-CMV-hNAGLUop Gene for Patients With Mucopolysaccharidosis (MPS) IIIB
NCT07818759
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +10 more
- Locations
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- Washington University School of Medicine Division of Genetics and Genomic Medicine, Rare Diseases Department of Pediatrics St Louis, Missouri, United States