NCT02544022
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +17 more
- Locations
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- Children's National Medical Center Washington D.C., District of Columbia, United States
- University of Chicago Chicago, Illinois, United States
- Johns Hopkins University Baltimore, Maryland, United States
- National Institutes of Health Clinical Center Bethesda, Maryland, United States