Active, Not Recruiting
Investigation of Individualised Antisense Oligonucleotides (ASOs) in People With Unique Genetic Variants Causing Severely Debilitating, Life Threatening (SDLT) Central Nervous System (CNS) Conditions
NCT07410143
- Conditions
- Pediatric SDLT CNS Disorders
- Locations
-
- Great Ormond Street Hospital London, United Kingdom