Active, Not Recruiting
A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
NCT03199469
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
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- UCLA Medical Center Los Angeles, California, United States
- Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- National Institute of Neurological Disorders and Stroke/NIH Porter Bethesda, Maryland, United States
- Hospital for Sick Children Toronto, Ontario, Canada