Enrolling by invitation
Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1
NCT05614531
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- The Children's Hospital of Fudan University Shanghai, Shanghai Municipality, China
- The Children'S Hospital Zhejiang University of Medicine Hangzhou, Zhejiang, China