Enrolling by invitation
Personalized Antisense Oligonucleotide Therapy for Participants With TARDBP ALS
NCT07743268
- Conditions
- Amyotrophic Lateral Sclerosis, Amyotrophic Lateral Sclerosis (ALS), Central Nervous System Diseases, +9 more
- Locations
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- Washington University St Louis, Missouri, United States
- Columbia University, Irving Medical Center New York, United States