NCT03633058
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
- Locations
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- University of Alabama Birmingham School of Medicine Birmingham, Alabama, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Rush University Medical Center Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States