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Clinical trial condition

Muscular Disorders, Atrophic

Explore clinical trials studying Muscular Disorders, Atrophic. Study availability and eligibility vary by location and protocol.

41 public trials 8 recruiting studies
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Muscular Disorders, Atrophic trial results

Enrolling by invitation

A Study of Long-term Safety and Efficacy of VX-670 in Participants With Myotonic Dystrophy Type I

NCT06926621

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
Locations
  • Wesley Research Institute Auchenflower, Australia
  • Neuroscience Clinical Trials Unit, Alfred Brain Melbourne, Australia
  • Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg - Pulmonology Leuven, Belgium
  • Altasciences Montreal Montreal, Canada
View all 15 locations
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Active, not recruiting

A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy

NCT05126758

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +7 more
Locations
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Arkansas Children's Hospital Little Rock, Arkansas, United States
  • UCSD Altman Clinical and Translational Research Institute La Jolla, California, United States
  • Children's Hospital of Los Angeles, Division of Neurology Los Angeles, California, United States
View all 20 locations
View Trial Details
Active, not recruiting

A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)

NCT06185764

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +15 more
Locations
  • Stanford Neuromuscular Research San Carlos, California, United States
  • University of Florida Clinical Research Center Gainesville, Florida, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
  • Boston Children's Hospital Boston, Massachusetts, United States
View all 26 locations
View Trial Details
Completed

Extension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients

NCT05479981

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +11 more
Locations
  • University of California Los Angeles Los Angeles, California, United States
  • Stanford University Palo Alto, California, United States
  • University of Colorado Denver, Colorado, United States
  • University of Florida Gainesville, Florida, United States
View Trial Details
Completed

Long-Term Outcomes of Ataluren in Duchenne Muscular Dystrophy

NCT03179631

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +8 more
Locations
  • Phoenix Childrens Hospital Phoenix, Arizona, United States
  • Children's Hospital of Los Angeles Los Angeles, California, United States
  • University of California, San Francisco (UCSF) - Benioff Children's Hospital - Oakland Oakland, California, United States
  • Stanford University Medical Center Palo Alto, California, United States
View all 64 locations
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Completed

Safety, Tolerability, PK, and PD Study of PGN-EDODM1 in Participants With Myotonic Dystrophy Type 1

NCT06204809

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more
Locations
  • UCI Center for Clinical Research Irvine, California, United States
  • Stanford University Palo Alto, California, United States
  • Rare Disease Research Atlanta, Georgia, United States
  • University of Kansas Medical Center Fairway, Kansas, United States
View Trial Details

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