Active, Not Recruiting
A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a Possible Treatment for Limb Girdle Muscular Dystrophy 2E/R4
NCT06246513
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Limb-girdle Muscular Dystrophy, +7 more
- Locations
-
- University of California, San Diego-Altman Clinical and Translational Research Institute La Jolla, California, United States
- Nationwide Childrens Hospital Columbus, Ohio, United States
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Children's Hospital of The King's Daughter Norfolk, Virginia, United States