Active, Not Recruiting
Microdystrophin Gene Transfer Study in Adolescents and Children With DMD
NCT03368742
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, Genetic Diseases, Inborn, +8 more
- Locations
-
- David Geffen School of Medicine at UCLA Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States