Active, Not Recruiting
Phase 3 Efficacy and Safety Study of GTX-102 in Pediatric Subjects With Angelman Syndrome (AS)
NCT06617429
- Conditions
- Abnormalities, Multiple, Angelman Syndrome, Central Nervous System Diseases, +7 more
- Locations
-
- Cedars Sinai Los Angeles, California, United States
- UCSD, Rady Children's Hospital San Diego, California, United States
- UCSF San Francisco, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States