NCT07432880
- Conditions
- Methylmalonic Acidemia (MMA), Methylmalonic acidemia
- Locations
-
- CHOP (Children's hospital of Philadelphia) Philadelphia, Pennsylvania, United States
- UPMC (Children's hospital of Pittsburgh) Pittsburgh, Pennsylvania, United States
- OSR_San Raffaele Milan, Italy
- OBGP (Bambino Gesu Ospedale Pediatrico) Roma, Italy