Active, Not Recruiting
Open-Label Extension Study of BBP-418 (Ribitol) for LGMD2I/R9
NCT07678775
- Conditions
- Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I), Muscular Dystrophy, Limb-Girdle, Type 2I
- Locations
-
- Arkansas Children's Hospital Little Rock, Arkansas, United States
- University of California Irvine Medical Center Orange, California, United States
- University of Colorado Hospital (UCH) - Anschutz Medical Campus Aurora, Colorado, United States
- University of Florida Health Center for Pediatric Neuromuscular and Rare Diseases Gainesville, Florida, United States