Active, Not Recruiting
A Phase 1/2/3 Study of UX701 Gene Therapy in Adults With Wilson Disease
NCT04884815
- Conditions
- Basal Ganglia Diseases, Brain Diseases, Brain Diseases, Metabolic, +16 more
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Stanford University Redwood City, California, United States
- University of California Davis Sacramento, California, United States
- Northwestern University Chicago, Illinois, United States