Active, Not Recruiting
A Study to Assess Safety and Efficacy of Avalglucosidase Alfa Administered Every Other Week in Pediatric Patients With Infantile-onset Pompe Disease Previously Treated With Alglucosidase Alfa
NCT03019406
- Conditions
- Glycogen Storage Disease Type II-Pompe's Disease
- Locations
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- Regional Medical Genetics Center of New York Site Number : 8400002 Valhalla, New York, United States
- Duke University Medical Center Site Number : 8400001 Durham, North Carolina, United States
- Seattle Childrens Hospital and Regional Medical Center- Site Number : 8400005 Seattle, Washington, United States
- Investigational Site Number : 2500004 Nantes, France