Active, Not Recruiting
Personalized Antisense Oligonucleotide for A Single Participant With ATN1 Gene Mutation
NCT07084311
- Conditions
- Brain Diseases, Central Nervous System Diseases, Dentatorubral-Pallidoluysian Atrophy, +6 more
- Locations
-
- Hawaii Pacific Neuroscience Honolulu, Hawaii, United States