Enrolling by Invitation
Long Term Follow-Up for RGX-111
NCT06103487
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +9 more
- Locations
-
- Children's Hospital of Orange County Orange, California, United States
- Hospital de Clinicas de Porto Alegre Porto Alegre, Rio Grande do Sul, Brazil