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Clinical trial condition

Congenital, Hereditary, and Neonatal Diseases and Abnormalities

Explore clinical trials studying Congenital, Hereditary, and Neonatal Diseases and Abnormalities. Study availability and eligibility vary by location and protocol.

18,481 public trials 3,141 recruiting studies
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Congenital, Hereditary, and Neonatal Diseases and Abnormalities trial results

Terminated

A Fabry Disease Gene Therapy Study

NCT04040049

Conditions
Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
Locations
  • Kaiser Permanente Los Angeles, California, United States
  • Columbia University New York, United States
  • UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
  • Lysosomal and Rare Disorders Research and Treatment Center Fairfax, Virginia, United States
View all 13 locations
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Terminated

A Study of Nivolumab-relatlimab Fixed-dose Combination Versus Regorafenib or TAS-102 in Participants With Later-lines of Metastatic Colorectal Cancer

NCT05328908

Conditions
Brain Diseases, Central Nervous System Diseases, Cerebellar Diseases, +18 more
Locations
  • Local Institution - 0044 Springdale, Arkansas, United States
  • Local Institution - 0012 Los Angeles, California, United States
  • Local Institution - 0117 Norwich, Connecticut, United States
  • Local Institution - 0025 Miami, Florida, United States
View all 139 locations
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Terminated

AVAST Anomalies Vasculaires Associées au Syndrome de Turner (Vascular Abnormalities Associated With Turner Syndrome)

NCT02250456

Conditions
Cardiovascular Abnormalities, Cardiovascular Diseases, Chromosome Disorders, +25 more
Locations
  • Service de Chirurgie et Médecine Vasculaire, CHU Jean Minjoz Besançon, France
  • Service d'Angiologie, CHU Bocage Dijon, France
  • Service de gynécologie, Centre Médico Chirurgical Obstétrical, Hôpitaux Universitaires Schiltigheim, France
  • Service d'endocrinologie, Hôpital Civil, Hôpitaux Universitaires Strasbourg, France
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Terminated

Dose-ranging Study of Oral PHA-022121 for Prophylaxis Against Angioedema Attacks in Patients With Hereditary Angioedema Type I or Type II

NCT05047185

Conditions
Angioedema, Angioedemas, Hereditary, C1 Esterase Inhibitor Deficiency, +23 more
Locations
  • Study site Birmingham, Alabama, United States
  • Study site Paradise Valley, Arizona, United States
  • Study site St Louis, Missouri, United States
  • Study Site Vienna, Austria
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Terminated

Efficacy and Safety of REC-2282 in Patients With Progressive Neurofibromatosis Type 2 (NF2) Mutated Meningiomas

NCT05130866

Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Cranial Nerve Diseases, Cranial Nerve Neoplasms, +25 more
Locations
  • House Institute Los Angeles, California, United States
  • University of California Los Angeles Los Angeles, California, United States
  • Children's National Hospital Washington D.C., District of Columbia, United States
  • University of Florida Gainesville, Florida, United States
View all 15 locations
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