Enrolling by Invitation
An Individual Patient, Open Label Study to Use ACER-001 to Treat Combined D,L-2 Hydroxyglutaric Aciduria (C-2HGA)
NCT07125066
- Conditions
- Combined D,L-2-hydroxyglutaric Aciduria
- Locations
-
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States