Active, Not Recruiting
Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT
NCT05739643
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +20 more
- Locations
-
- Children's Hospital of Orange County (CHOC) Orange, California, United States
- University of Michigan Hospitals - Michigan Medicine Ann Arbor, Michigan, United States
- Duke University Medical Center Durham, North Carolina, United States