Active, Not Recruiting
A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
NCT05166161
- Conditions
- Amino Acid Metabolism, Inborn Errors, Brain Diseases, Brain Diseases, Metabolic, +10 more
- Locations
-
- Children's Hospital Colorado Aurora, Colorado, United States
- UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism Gainesville, Florida, United States
- Indiana University School of Medicine Department of Medical and Molecular Genetics Indianapolis, Indiana, United States
- Boston Children's Hospital Boston, Massachusetts, United States