Enrolling by Invitation
A Phase 1b Study of Adenylosuccinic Acid (ASA-001) for Adenylosuccinate Synthase 1 (ADSS1) Deficient Myopathy.
NCT07412821
- Conditions
- Adenylosuccinate Synthase 1 Deficient Myopathy
- Locations
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- University of California Los Angeles (UCLA) Los Angeles, California, United States