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Published and searchable clinical trials
NCT03937817
- Conditions
- Alpha and Beta Thalassemia, Anemia, Anemia, Hemolytic, +17 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Long-term Follow-up Study of BRL-101 for TDT
NCT06298630
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- Nanfang Hospital, Southern Medical University Guangzhou, Guangdong, China
- Sun Yat-Sen Memorial Hospital of Sun Yat-Sen University Guangzhou, Guangdong, China
- Shenzhen Children 's Hospital Shenzhen, Guangdong, China
- No. 923 Hospital of Joint Support Force of Chinese People 's Liberation Army Hospital Nanning, Guangxi, China
NCT07599176
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Study of Safety & PK of Luspatercept (ACE-536) in Pediatric Participants With Beta (β)-Thalassemia
NCT04143724
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
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- Local Institution - 601 Los Angeles, California, United States
- New York Presbyterian Hospital New York, United States
- Southern Medical University Nanfang Hospital Guangzhou, Guangdong, China
- Shenzhen Second People's Hospital Shenzhen, Guangdong, China
NCT03653338
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +18 more
- Locations
-
- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
NCT04064060
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +13 more
- Locations
-
- Local Institution - 968 Los Angeles, California, United States
- Local Institution - 971 Oakland, California, United States
- Local Institution - 978 Stanford, California, United States
- Local Institution - 975 Tampa, Florida, United States
NCT05736419
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
-
- Memorial Sloan Kettering at Basking Ridge (Consent only) Basking Ridge, New Jersey, United States
- Memorial Sloan Kettering Monmouth (Consent only) Middletown, New Jersey, United States
- Memorial Sloan Kettering Bergen (Consent only) Montvale, New Jersey, United States
- Memorial Sloan Kettering Suffolk - Commack (Consent only) Commack, New York, United States
NCT06364774
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
-
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
NCT05735717
- Conditions
- AML, Acute Leukemia, Acute Lymphoblastic Leukemia, +74 more
- Locations
-
- University of Minnesota Masonic Cancer Center Minneapolis, Minnesota, United States
NCT05477563
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +11 more
- Locations
-
- New York Presbyterian Hospital - Morgan Stanley Children's Hospital New York, United States
- Levine Children's Hospital - Hematology Charlotte, North Carolina, United States
- TriStar Medical Group Children's Specialists - Pediatric Oncology Nashville, Tennessee, United States
- University Hospital Dusseldorf - Department of Pediatric Oncology, Hematology and Clinical Immunology Düsseldorf, Germany
NCT06647979
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +12 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States
NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01245179
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +9 more
- Locations
-
- Augusta University Augusta, Georgia, United States
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
-
- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT06479616
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
-
- Children's Hospital of Fudan University Shanghai, Shanghai Municipality, China
NCT07112703
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +12 more
- Locations
-
- Zagazig university hospitals. Zagazig, Egypt
NCT04099966
- Conditions
- Acute Leukemia, Amegakaryocytic Thrombocytopenia, Anemia, +34 more
- Locations
-
- New York Medical College Valhalla, New York, United States
Safety and Efficacy of the Lentiviral Vector in Gene Therapy of Beta-thalassemia Patients
NCT06219239
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
-
- Institute of Hematology & Blood Diseases Hospital Tianjin, Tianjin Municipality, China
Unraveling the Impact of Thalidomide at Diverse Doses in Transfusion Dependent Beta Thalassemia
NCT06490627
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
-
- National Institute of blood disease and bone marrow transplant Karachi, Sindh, Pakistan
NCT06271512
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
-
- UCSF Benioff Children's Hospitals Oakland, California, United States
- Stanford University Palo Alto, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Cohen Children's Medical Center New Hyde Park, New York, United States