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Enrolling by Invitation
Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy
NCT06851767
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +9 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
Enrolling by Invitation
Natural History Study of SCID Disorders
NCT01186913
- Conditions
- ADA SCID, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, +17 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California, Los Angeles Los Angeles, California, United States