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NCT07433621
- Conditions
- Lymphoproliferative Syndrome, X-Linked, 2, XIAP Deficiency
- Locations
-
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
NCT03113760
- Conditions
- Lymphoproliferative Syndrome, X-Linked, 2, NLRC4-MAS, XIAP Deficiency
- Locations
-
- UCSD _ Department of Pediatrics / Rady Children's Hospital La Jolla, California, United States
- Children's Healthcare of Atlanta at Egleston Atlanta, Georgia, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
Completed
Therapeutic Use of Tadekinig Alfa in NLRC4 Mutation and XIAP Deficiency As Open Label Extension
NCT03512314
- Conditions
- Lymphoproliferative Syndrome, X-Linked, 2, NLRC4-MAS, XIAP Deficiency
- Locations
-
- UCSD _ Department of Pediatrics / Rady Children's Hospital La Jolla, California, United States
- Shands Children's Hospital Gainsville, Florida, United States
- Children's Healthcare of Atlanta at Egleston Atlanta, Georgia, United States
- Boston Children's Hospital Boston, Massachusetts, United States