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NCT06581146
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
-
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Recruiting
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
NCT07052929
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
-
- Lurie Children's Hospital Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Oregon Health & Science University Portland, Oregon, United States
- The Hospital for Sick Children Toronto, Ontario, Canada
NCT02704273
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
-
- UCLA Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- National Institute of Neurological Disorders and Stroke/NIH Porter Bethesda, Maryland, United States
NCT02453152
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
-
- University of Florida Gainesville, Florida, United States
Completed
Myotubular Myopathy Event Study
NCT01840657
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +8 more
- Locations
-
- CMDIR Torrance, California, United States
Active, Not Recruiting
A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
NCT03199469
- Conditions
- Muscular Diseases, Musculoskeletal Diseases, Myopathies, Structural, Congenital, +3 more
- Locations
-
- UCLA Medical Center Los Angeles, California, United States
- Ann & Robert H Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- National Institute of Neurological Disorders and Stroke/NIH Porter Bethesda, Maryland, United States
- Hospital for Sick Children Toronto, Ontario, Canada