Enrolling by Invitation Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy NCT06851767 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +9 more Locations National Institutes of Health Clinical Center — Bethesda, Maryland, United States View Trial Details