Enrolling by Invitation Base-Edited Hematopoietic Stem/Progenitor Cell X-Linked Severe Combined Immunodeficiency Gene Therapy NCT06851767 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +9 more Locations National Institutes of Health Clinical Center — Bethesda, Maryland, United States View Trial Details
Completed Gene Therapy for X-linked Severe Combined Immunodeficiency NCT01410019 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Genetic Diseases, X-Linked, +8 more Locations Hopital Necker — Paris, France View Trial Details
Completed Total-Body Irradiation Followed By Cyclosporine and Mycophenolate Mofetil in Treating Patients With Severe Combined Immunodeficiency Undergoing Donor Bone Marrow Transplant NCT00008450 Conditions Adenosine Deaminase Deficiency, Autosomal Recessive Disorder, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more Locations Fred Hutch/University of Washington Cancer Consortium — Seattle, Washington, United States View Trial Details