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Long-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
NCT02698579
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +24 more
- Locations
-
- Mattel Children's Hospital-UCLA Los Angeles, California, United States
- Lucile Packard Children's Hospital - Stanford Palo Alto, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States