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NCT02841553
- Conditions
- Abnormalities, Multiple, Ataxia, Blindness, +40 more
- Locations
-
- Washington University School of Medicine St Louis, Missouri, United States
Recruiting
Monogenic Diabetes Misdiagnosed as Type 1
NCT03988764
- Conditions
- Abnormalities, Multiple, Autoimmune Diseases, Blindness, +43 more
- Locations
-
- The Montreal Children's Hospital Montreal, Quebec, Canada
Not Yet Recruiting
Does Recessive Optic Atrophy Due to WFS1 Exist?
NCT07336966
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +36 more
- Locations
-
Not specified
Not Yet Recruiting
Mechanisms of Fecal Incontinence in Wolfram Syndrome
NCT07313085
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +40 more
- Locations
-
- HEGP Paris, France
NCT03717909
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +35 more
- Locations
-
- CHU de Montpellier, Hopital Gui de Chauliac Montpellier, France
- Hôpital Européen Georges-Pompidou Paris, France
- Medical University of Lodz Lodz, Poland
- Unidad de Gestión Clínica Almería Periferia. Distrito Sanitario Almería Almería, Spain
NCT03951298
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +37 more
- Locations
-
- Washington University School of Medicine St Louis, Missouri, United States
Completed
A Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome
NCT02829268
- Conditions
- Abnormalities, Multiple, Ataxia, Blindness, +40 more
- Locations
-
- Washington University School of Medicine St Louis, Missouri, United States
NCT02455414
- Conditions
- Abnormalities, Multiple, Autoimmune Diseases, Blindness, +38 more
- Locations
-
- Washington University School of Medicine St Louis, Missouri, United States
Active, Not Recruiting
AMX0035 in Adult Patients With Wolfram Syndrome
NCT05676034
- Conditions
- Abnormalities, Multiple, Blindness, Congenital Abnormalities, +35 more
- Locations
-
- Washington University St Louis, Missouri, United States