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Conditions
3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
Locations
  • CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +14 more
Locations
  • Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy

NCT04429568

Conditions
Behavior, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +34 more
Locations
  • Zuckerberg San Francisco General Hospital San Francisco, California, United States
  • University of California, San Francisco San Francisco, California, United States
Conditions
Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +51 more
Locations
  • Children's Hospital Colorado Aurora, Colorado, United States
  • Oregon Health and Science University Portland, Oregon, United States
  • Vanderbilt University/Ingram Cancer Center Nashville, Tennessee, United States
  • Seattle Children's Hospital Seattle, Washington, United States
Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Great Ormond Street Hospital London, United Kingdom
  • Royal Free Hospital London, United Kingdom
Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Department of Pediatrics, University of Alabama at Birmingham Birmingham, Alabama, United States
  • Phoenix Children's Hospital Phoenix, Arizona, United States
  • Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Keck School of Medicine, University of Southern California Los Angeles, California, United States
  • Department of Pediatrics, David Geffen School of Medicine at University of California, Los Angeles, Los Angeles, California, United States
View all 43 locations

NCT01347346

Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
Locations
  • Hôpital Necker-Enfants Malades Paris, France
Conditions
Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
Locations
  • Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
  • Hospital of the University of Pennsylvania Philadelphia, Pennsylvania, United States
  • The Texas Children's Hospital Houston, Texas, United States