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Published and searchable clinical trials
NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
Analysis of the Therapeutic and Clinical Profile of Cannabinoid Treatments: A Real-World Study
NCT07362407
- Conditions
- Anxiety Disorders, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +34 more
- Locations
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- Universidade Federal de Santa Catarina (UFSC), Centro de Ciências Biológicas (CCB), Campus Universitário, Trindade, Florianópolis - SC. Florianópolis, Santa Catarina, Brazil
Sequential Cadaveric Lung and Bone Marrow Transplant for Immune Deficiency Diseases
NCT01852370
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Chronic Disease, +35 more
- Locations
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- Children's Hospital of Pittsburgh of UPMC Pittsburgh, Pennsylvania, United States
NCT01410825
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Children's Hospital Boston Boston, Massachusetts, United States
Baby Detect : Genomic Newborn Screening
NCT05687474
- Conditions
- 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
- Locations
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- CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
NCT01515462
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +14 more
- Locations
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- Ospedale San Raffaele - Telethon Institute for Gene Therapy (OSR-TIGET) Milan, Italy
THC Crossover Study
NCT04429568
- Conditions
- Behavior, Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, +34 more
- Locations
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- Zuckerberg San Francisco General Hospital San Francisco, California, United States
- University of California, San Francisco San Francisco, California, United States
NCT03513328
- Conditions
- Acquired Anemia Hemolytic, Acquired Neutropenia in Newborn, Acquired Thrombocytopenia, +82 more
- Locations
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- UF Health Shands Children's Hospital Gainesville, Florida, United States
NCT01953016
- Conditions
- APECED, Autoimmune Diseases, Blood Coagulation Disorders, +20 more
- Locations
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- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT00919503
- Conditions
- Anemia, Anemia, Aplastic, Anemia, Diamond-Blackfan, +51 more
- Locations
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- Children's Hospital Colorado Aurora, Colorado, United States
- Oregon Health and Science University Portland, Oregon, United States
- Vanderbilt University/Ingram Cancer Center Nashville, Tennessee, United States
- Seattle Children's Hospital Seattle, Washington, United States
NCT01347242
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Great Ormond Street Hospital London, United Kingdom
- Royal Free Hospital London, United Kingdom
NCT04350164
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Dmitry Rogachev National Research Center of Pediatric Hematology, Oncology and Immunology Moscow, Russia
NCT02064933
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Department of Pediatrics, University of Alabama at Birmingham Birmingham, Alabama, United States
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Cancer and Blood Disease Institute, Children's Hospital Los Angeles, Keck School of Medicine, University of Southern California Los Angeles, California, United States
- Department of Pediatrics, David Geffen School of Medicine at University of California, Los Angeles, Los Angeles, California, United States
NCT01917708
- Conditions
- Albinism, Anemia, Anemia, Aplastic, +80 more
- Locations
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- Children's Healthcare of Atlanta Atlanta, Georgia, United States
NCT01529827
- Conditions
- Accelerated Phase Chronic Myelogenous Leukemia, Adult Acute Lymphoblastic Leukemia in Remission, Adult Acute Myeloid Leukemia With 11q23 (MLL) Abnormalities, +179 more
- Locations
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- Roswell Park Cancer Institute Buffalo, New York, United States
NCT03399461
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- GSK Investigational Site Collegeville, Pennsylvania, United States
Gene Therapy for WAS
NCT01347346
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +13 more
- Locations
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- Hôpital Necker-Enfants Malades Paris, France
NCT00774358
- Conditions
- Blood Coagulation Disorders, Blood Coagulation Disorders, Inherited, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +16 more
- Locations
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- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- Hospital of the University of Pennsylvania Philadelphia, Pennsylvania, United States
- The Texas Children's Hospital Houston, Texas, United States
NCT00086476
- Conditions
- Albinism, Albinism, Oculocutaneous, Amino Acid Metabolism, Inborn Errors, +36 more
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States