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A Long-Term Follow-Up Study of Participants With Sickle Cell Disease or Transfusion Dependent β-Thalassemia Who Received EDIT-301
NCT06363760
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
-
- UCSF Benioff Children's Hospital Oakland, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Smilow Cancer Hospital New Haven, Connecticut, United States
- Johns Hopkins All Children's Hospital St. Petersburg, Florida, United States
Active, Not Recruiting
A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)
NCT04770779
- Conditions
- Transfusion-dependent Alpha-Thalassemia, Transfusion-dependent Beta-Thalassemia
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- San Diego Hospital, UC San Diego Health La Jolla, California, United States
- Children's Hospital Oakland Oakland, California, United States
- Stanford Medicine Palo Alto, California, United States
Active, Not Recruiting
Long-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Therapy
NCT02633943
- Conditions
- Transfusion-dependent Beta-Thalassemia
- Locations
-
- Oakland, California, United States
- Chicago, Illinois, United States
- Bethesda, Maryland, United States
- New York, United States