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Enrolling by Invitation
Decision-Making and Quality of Life Surrounding Hematologic Disease and Gene Therapy
NCT06664541
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +8 more
- Locations
-
- Georgetown University Medical Center Washington D.C., District of Columbia, United States
Active, Not Recruiting
EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)
NCT05444894
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
-
- University of California San Francisco Oakland, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Columbia University Medical Center - Department of Pediatrics New York, United States
- Columbia University Medical Center New York, United States