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EDIT-301 for Autologous Hematopoietic Stem Cell Transplant (HSCT) in Participants With Transfusion-Dependent Beta Thalassemia (TDT)
NCT05444894
- Conditions
- Anemia, Anemia, Hemolytic, Anemia, Hemolytic, Congenital, +10 more
- Locations
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- University of California San Francisco Oakland, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Columbia University Medical Center - Department of Pediatrics New York, United States
- Columbia University Medical Center New York, United States