Recruiting Natural History of Acquired and Inherited Bone Marrow Failure Syndromes NCT05012111 Conditions Anemia, Anemia, Aplastic, Bone Marrow Diseases, +9 more Locations National Institutes of Health Clinical Center — Bethesda, Maryland, United States View Trial Details
Recruiting Nucleoside Therapy in Patients With Telomere Biology Disorders NCT06817590 Conditions Bone Marrow Diseases, Bone Marrow Failure Disorders, Congenital Abnormalities, +26 more Locations Boston Childrens Hospital — Boston, Massachusetts, United States View Trial Details
Recruiting Alpha/Beta TCD HCT in Patients With Inherited BMF Disorders NCT03579875 Conditions Anemia, Anemia, Aplastic, Anemia, Hypoplastic, Congenital, +24 more Locations Masonic Cancer Center at University of Minnesota — Minneapolis, Minnesota, United States View Trial Details
Completed Needs Assessment for Individuals and Families Affected by Dyskeratosis Congenita (DC) and Related Telomere Biology Disorders (TBD) NCT04959188 Conditions Bone Marrow Diseases, Bone Marrow Failure Disorders, Congenital Abnormalities, +12 more Locations National Cancer Institute (NCI) — Bethesda, Maryland, United States View Trial Details