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NCT00383448
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
NCT00176904
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Completed
Gene Therapy for Tay-Sachs Disease
NCT01869270
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- Data Management and Coordinating Center (DMCC), Univ. of South Florida Tampa, Florida, United States
- University of Minnesota Minneapolis, Minnesota, United States
Active, Not Recruiting
Long-Term Follow-Up of Subjects Treated With AXO-AAV-GM2 for Tay-Sachs or Sandhoff Disease
NCT06614569
- Conditions
- Brain Diseases, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, +19 more
- Locations
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- UMass Chan Medical School Worcester, Massachusetts, United States