Recruiting Myotonic Dystrophy Family Registry NCT02398786 Conditions Congenital Myotonic Dystrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dystrophia Myotonica, +24 more Locations Myotonic Dystrophy Foundation — Oakland, California, United States View Trial Details
Enrolling by Invitation Global Open-Label Extension Study of Del-desiran for the Treatment of DM1 NCT07008469 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +19 more Locations University of California, Los Angeles (UCLA) — Los Angeles, California, United States Stanford University — Stanford, California, United States University of Colorado — Denver, Colorado, United States University of Florida — Gainesville, Florida, United States View all 35 locations View more locations Show fewer locations Loading locations... View Trial Details
Completed Longitudinal Evaluation of Neuromuscular Involvement in Type 1 Myotonic Dystrophy NCT07362316 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, Heredodegenerative Disorders, Nervous System, +10 more Locations Centre de recherche du CHU de Québec-Université Laval — Laval, Canada Institut de Myologie — Paris, Île-de-France Region, France View Trial Details