Recruiting Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1 NCT07486934 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Genetic Diseases, Inborn, +18 more Locations UCSD - Altman Clinical and Translational Research Institute — La Jolla, California, United States Rare Disease Research, LLC — Atlanta, Georgia, United States IU Health Neuroscience Center — Indianapolis, Indiana, United States Roy Blunt NextGen Precision Health Institute — Columbia, Missouri, United States View all 24 locations View more locations Show fewer locations Loading locations... View Trial Details
Active, Not Recruiting Global Study of Del-desiran for the Treatment of DM1 NCT06411288 Conditions Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DM1, Dystrophy Myotonic, +21 more Locations Stanford University — Stanford, California, United States University of Colorado — Denver, Colorado, United States University of Florida — Gainesville, Florida, United States University Research Center of South Florida — Tampa, Florida, United States View all 34 locations View more locations Show fewer locations Loading locations... View Trial Details