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Published and searchable clinical trials
NCT07047144
- Conditions
- Anti-myostatin, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
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- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital of Orange County (CHOC) Orange, California, United States
- Stanford Neuroscience Health Center (SNHC) Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
NCT06839469
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy (DMD), +16 more
- Locations
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- Stanford University Palo Alto, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Columbia University Irving Medical Center New York, United States
Gait and Bone Health in SMA
NCT07400198
- Conditions
- Ambulatory Spinal Muscular Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
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- Columbia University Irving Medical Center New York, United States
NCT05430113
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
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- University of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT05156320
- Conditions
- Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
- Locations
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- Children's of Alabama Birmingham, Alabama, United States
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital of Los Angeles Los Angeles, California, United States
- Stanford University Medical Center Palo Alto, California, United States
NCT05089656
- Conditions
- Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
- Locations
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- Connecticut Children's Medical Center Farmington, Connecticut, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- Clinic for Special Children Strasburg, Pennsylvania, United States
- St Jude Children's Research Hospital Memphis, Tennessee, United States
An Active Treatment Study of SRK-015 in Patients With Type 2 or Type 3 Spinal Muscular Atrophy
NCT03921528
- Conditions
- Atrophy, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
- Locations
-
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Stanford University Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- The Johns Hopkins University Baltimore, Maryland, United States
NCT06632730
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +10 more
- Locations
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- Novartis Pharmaceuticals East Hanover, New Jersey, United States
NCT04193085
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne Muscular Dystrophy, +16 more
- Locations
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- Columbia University Medical Center New York, United States
NCT05715749
- Conditions
- Behavior, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +12 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
NCT02122952
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- Nationwide Children's Hospital Columbus, Ohio, United States
NCT02895789
- Conditions
- Behavior, Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +18 more
- Locations
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- Columbia University Medical Center New York, United States
International SMA Patient Registry
NCT00466349
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +8 more
- Locations
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- Indiana University School of Medicine Indianapolis, Indiana, United States
CARNIVAL Type I: Valproic Acid and Carnitine in Infants With Spinal Muscular Atrophy (SMA) Type I
NCT00661453
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- Johns Hopkins University Baltimore, Maryland, United States
- Children's Hospital of Michigan Detroit, Michigan, United States
- Duke University Medical Center Durham, North Carolina, United States
- Ohio State University Medical Center, Dept. of Neurology Columbus, Ohio, United States
NCT00756821
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- Stanford University Stanford, California, United States
- The Children's Hospital Aurora, Colorado, United States
- University of Iowa Iowa City, Iowa, United States
Spinal Cord Stimulation for the Treatment of Motor Deficits in People With Spinal Muscular Atrophy - Upper Limb
NCT06300996
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +14 more
- Locations
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- University of Pittsburgh Pittsburgh, Pennsylvania, United States
Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of Apitegromab
NCT05626855
- Conditions
- Anti-myostatin, Atrophy, Central Nervous System Diseases, +20 more
- Locations
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- Phoenix Childrens Hospital Phoenix, Arizona, United States
- UCSD Altman Clinical and Translational Research La Jolla, California, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- Stanford Neuroscience Health Center Palo Alto, California, United States
Long-Term Follow-up Study for Patients From AVXS-101-CL-101
NCT03421977
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +9 more
- Locations
-
- Nationwide Children's Hospital Columbus, Ohio, United States
Long-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
NCT04042025
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +12 more
- Locations
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- Stanford University Medical Center Palo Alto, California, United States
- Children's Hospital Colorado Aurora, Colorado, United States
- Ann Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- John Hopkins Hospital - David M. Rubenstein Child Health Building Baltimore, Maryland, United States
Spinraza in Adult Spinal Muscular Atrophy
NCT03709784
- Conditions
- Central Nervous System Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Genetic Diseases, Inborn, +11 more
- Locations
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- Barrow Neurological Institute Phoenix, Arizona, United States
- Georgetown University Washington D.C., District of Columbia, United States
- Johns Hopkins Baltimore, Maryland, United States
- Massachusetts General Hospital-Harvard University Boston, Massachusetts, United States