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NCT03604835
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +12 more
- Locations
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- Children's Hospital of Orange County Orange, California, United States
- Children's National Health System Washington D.C., District of Columbia, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago Chicago, Illinois, United States
- University of Michigan Ann Arbor, Michigan, United States
NCT02432144
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
- Locations
-
- Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Orange County Orange, California, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Baylor College of Medicine Houston, Texas, United States
NCT02230566
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +17 more
- Locations
-
- Children's Hospital Oakland Oakland, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Miami Children's Hospital Miami, Florida, United States
- University of Minnesota Minneapolis, Minnesota, United States
NCT02418455
- Conditions
- Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Connective Tissue Diseases, +16 more
- Locations
-
- Children's National Health System Washington D.C., District of Columbia, United States
- New York University Langone Medical Center New York, United States
- University of Utah Hospital Salt Lake City, Utah, United States
- Centro Hospitalar do Porto Porto, Portugal
NCT01043640
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more
- Locations
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- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States
Active, Not Recruiting
MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
- Conditions
- Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more
- Locations
-
- Masonic Cancer Center, University of Minnesota Minneapolis, Minnesota, United States