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Published and searchable clinical trials
NCT05432310
- Conditions
- Adenosine Deaminase Severe Combined Immune Deficiency, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
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- University of California, Los Angeles (UCLA) Los Angeles, California, United States
An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID
NCT04049084
- Conditions
- Adenosine Deaminase Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, +10 more
- Locations
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- Mattel Children's Hospital UCLA/Ronald Reagan UCLA Medical Center Los Angeles, California, United States
- UCL Great Ormond Street Institute of Child Health London, United Kingdom
Natural History Study of SCID Disorders
NCT01186913
- Conditions
- ADA SCID, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, +17 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- Phoenix Children's Hospital Phoenix, Arizona, United States
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California, Los Angeles Los Angeles, California, United States
NCT03878069
- Conditions
- Adenosine Deaminase Severe Combined Immunodeficiency, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
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- University of California Los Angeles Los Angeles, California, United States
- Allergy & Asthma Medical Group and Research Center, A P.C. San Diego, California, United States
- UCSF - University of California San Francisco, California, United States
- Children's National Washington D.C., District of Columbia, United States
NCT01852071
- Conditions
- ADA-SCID, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
-
- Mattel Children's Hospital, UCLA Los Angeles, California, United States
- Mark O. Hatfield Clinical Research Center, NIH Bethesda, Maryland, United States
NCT02999984
- Conditions
- Severe Combined Immunodeficiency Due to ADA Deficiency, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
-
- University of California, Los Angeles Los Angeles, California, United States
NCT00043225
- Conditions
- Bacterial Infections, Bacterial Infections and Mycoses, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +19 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States
- University of Washington Seattle, Washington, United States
- University of Wisconsin Madison, Wisconsin, United States
- Medical College of Wisconsin Milwaukee, Wisconsin, United States
NCT00794508
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Genetic Diseases, Inborn, +8 more
- Locations
-
- University of California, Los Angeles Los Angeles, California, United States
EZN-2279 in Patients With ADA-SCID
NCT01420627
- Conditions
- ADA-SCID, Adenosine Deaminase Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
-
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California San Francisco San Francisco, California, United States
- National Jewish Health Denver, Colorado, United States
- UBMD Buffalo, New York, United States
NCT00018018
- Conditions
- Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, Genetic Diseases, Inborn, +10 more
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States