Skip to main content
OpenTrials

Clinical trial discovery

Find Clinical Trials

Search studies by condition, treatment, location, eligibility, or trial identifier.

Showing 1–2 of 2 trials

Active filters

Clinical trials found

Published and searchable clinical trials

Searching for clinical trials...
Conditions
Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gene Therapy, Genetic Diseases, Inborn, +8 more
Locations
  • Mattel Children's Hospital - UCLA Los Angeles, California, United States
  • Emory University/Childrens Healthcare of Atlanta Atlanta, Georgia, United States
  • Boston Childrens Hospital Boston, Massachusetts, United States
  • Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States

NCT03655223

Conditions
17 Alpha-Hydroxylase Deficiency, 3-Hydroxy-3-Methylglutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, +456 more
Locations
  • RTI International Research Triangle Park, North Carolina, United States